Duchenne Muscular Dystrophy Gene Therapy Trial Marks Milestone
REGENXBIO Inc. announced a dosing milestone in the Phase I/II AFFINITY DUCHENNE trial of RGX-202 for Duchenne muscular dystrophy.
REGENXBIO Inc. announced a dosing milestone in the Phase I/II AFFINITY DUCHENNE trial of RGX-202 for Duchenne muscular dystrophy.
Nyheim Hines will wear special cleats Dec. 1 to raise awareness of the Muscular Dystrophy Association for the My Cleats My Cause campaign.
Registration is open for the 2023 MDA Clinical & Scientific Conference, March 19-22, at the Hilton Anatole in Dallas and via live stream.
Cure Rare Disease announces the approval from the U.S. Food and Drug Administration to administer its very first therapeutic.
Read MoreParent Project Muscular Dystrophy expands their Certified Duchenne Care Center Program with the certification of the Billings Clinic.
Read MoreThe Oxford-Harrington Rare Disease Centre announce its support of a novel treatment for Duchenne muscular dystrophy.
Read MoreSarepta Therapeutics Inc announces its intent to submit a BLA seeking accelerated approval for SRP-9001 to treat individuals with Duchenne.
Read MoreCIONIC announces a collaboration with acclaimed designer Yves Behar and his world-renowned multidisciplinary design firm, fuseproject.
Read MoreParent Project Muscular Dystrophy adds the clinic at UPMC Children’s Hospital of Pittsburgh to its Certified Duchenne Care Center Program.
Read MoreFulcrum Therapeutics is using AMRA Medical’s muscle fat infiltration (MFI) as a secondary endpoint in its phase 3 FSHD clinical trial: REACH.
Read MoreParent Project Muscular Dystrophy expands its Certified Duchenne Care Program with the certification of the first clinic in St. Louis.
Read MoreMutations that cause Duchenne muscular dystrophy slow electrical activity in the heart, causing abnormal heart rhythms, a study notes.
Read MoreAMRA Medical publishes results of its Fulcrum-sponsored study highlighting the development and use of a MRI protocol for muscle analysis.
Read MoreParent Project Muscular Dystrophy nominates Duchenne to be part of Recommended Uniform Screening Panel (RUSP) for newborns.
Read MoreICD-10-CM codes for LGMD and several of its subtypes will be fully implemented and ready for use starting this October, MDA reports.
Read MoreAn existing cancer drug could have potential as a treatment for muscular dystrophy, researchers suggest in a new study.
Read MoreParent Project Muscular Dystrophy will host its 2022 Annual Conference in Scottsdale, Arizona, June 23-26.
Read MoreAvidity Biosciences Inc joins in activities to raise awareness for FSHD and highlights preclinical treatment results supporting AOC 1020.
Read More